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Innovations in Science
Agenda
Previous Sessions
Date | Time | Session Name |
---|---|---|
June 18 | 3:00 PM | Virtual Industry Forum: Presented by Sanofi Genzyme Respiratory Involvement in Neuromuscular Disorders: Pompe Disease as a Prototype Namita Goyal, MD Michelle Cao, DO |
June 19 | 4:00 PM | Small Molecules & Therapeutic Antibodies: Experimental, Preclinical, Clinical (Now Available On-Demand)
Stathmin-2 loss a new hallmark forTDP-43-dependent Amyotrophic Lateral Sclerosis VCP inhibitor CB-5083: a potential treatment for VCP inclusion Body Myopathy Inhibition of PKC alleviates nucleocytoplasmic transport disruption in FUS-mediated ALS “Designer DNA drug” therapies for sporadic ALS: restoration of stathmin-2oruse of “identity theft” to generate replacement neurons Update on Rare Disease Programs at Denali |
July 10 | 4:00 PM | Implications of NBS in Clinical Practice - What Does the Future Hold? (CME Certified) (Now Available On-Demand)
Session Moderator Newborn Screening for Neuromuscular Conditions Newborn Screening: How to Prepare Your MDA Care Center Newborn Screening for SMA: Wisconsin Experience |
July 17 | 4:00 PM | When Gut Feelings Aren’t Helping - Navigating Complicated Ethics in the Neuromuscular Clinic (CME Certified) (Now Available On-Demand) John Brandsema, MD (Chair) Alyssa Burgart, MD, MA Julie Parsons, MD Thomas Crawford, MD |
July 27 | 5:45 PM | Virtual Industry Forum: Presented by PTC (Now Available On-Demand) Duchenne Muscular Dystrophy: Examining the Totality of Evidence for Corticosteroid Treatment Vamshi Rao, MD (Chair) Perry Shieh, MD, PhD Armando Villalta, PhD |
July 28 | 4:00 PM | Virtual Industry Forum: Presented by Biogen Time to SHINE on SMA: The Nusinersen Clinical Development Program Including Long-Term Outcomes in Infants and Children Diana Castro, MD Thomas Crawford, MD |
July 31 | 4:00 PM | Ultra-Rare Myopathies and Dystrophies (Now Available On-Demand) Alan Beggs, PhD (Chair) Angela Lek, PhD (Chair) Frances Evesson, PhD Scot Wolfe, PhD Asli Aykanat, MD |
August 6 | 3:00 PM | Virtual Industry Forum: Presented by Biogen Later-onset SMA: Perception of Stability and a Treatment for a Neuromuscular Disease Crystal Proud, MD Molly Stark, DPT Kathleen McMahon, RN Patient Ambassador Dallas F. |
August 7 | 4:00 PM | Clinical Trial Design (CME Certified) (Now Available On-Demand)
Session Moderator Session Moderator Biostatistical considerations in clinical trial design in neuromuscular disorders Clinical considerations for efficient design of clinical trials for neuromuscular diseases “Common” neuromuscular diseases, with large-scale studies, using ALS as an example Rare neuromuscular disease considerations, using giant axonal neuropathy and myotubular myopathy as examples |
August 12 | 2:00 PM | Virtual Industry Forum: Presented by Sarepta Therapeutics Evolving Diagnostic Pathway & Gene Therapies in Development for the Limb-Girdle Muscular Dystrophies Matthew Wicklund, MD Eric Pozsgai, PhD Louise Rodino-Klapac, PhD |
August 14 | 4:00 PM | Lab to Life: What's New in ALS & CMT (Now Available On-Demand) Matthew Harms, MD (Chair) Michael Shy, MD (Chair) Stephan Zuchner, PhD |
August 19 | 4:00 PM | Best Practices in Communication in NMD (This program is offered for up to .15 (or 90 minutes) ASHA CEU's, Intermediate level, professional area) Angela Strauch Lane, M.S., CCC-SLP Kelly Casey, OTD, OTR/L, BCPR, ATP, CPAM |
August 20 | 12:00 PM | Virtual Industry Forum: Presented by Alexion Pharmaceuticals The Role of Complement in Neuromuscular Disorders Ahmed Enayetallah, MD PhD |
August 28 | 4:00 PM | Real World Data: Disease Registries, Natural History & Post-Marketing Surveillance (CME Certified) (Now Available On-Demand) Paul Mehta, MD (Chair) Paula Clemens, MD (Chair) Craig Campbell, MD Craig McDonald, MD Jane Larkindale, DPhil Jeff Rothstein, MD, PhD |
August 31 | 4:00 PM | Best Practices in Swallowing in ALS (This program is offered for up to 0.1 (or 60 minutes) of ASHA CEU's, Intermediate level, professional area) Donna C. Tippett, MPH, MA CCC-SLP |
September 11 | 2:00 PM | Preclinical Trial Design and Biomarker Development (Now Available On-Demand) Kanneboyina Nagaraju, DVM, PhD (Chair) Jim Dowling, MD (Chair) Laurent Bogdanik, PhD Yetrib Hathout, PhD Yi-Wen Chen, Ph.D., M.S., D.V.M |
September 14 | 2:00 PM |
Virtual Industry Forum: Presented by Sarepta Therapeutics Jahannaz Dastgir, DO |
September 18 | 3:00 PM | Lab to Life: What's New in LGMD, FSHD & DM (CME Certified) Charles Thornton, MD (Chair) Katherine Mathews, MD (Chair) Tom Cooper, MD Laura Ranum, PhD Katelyn Daman Steve Tapscott, MD, PhD Matthew Wicklund, MD Melissa Spencer, PhD |
September 21 | 3:00 PM | Virtual Industry Forum: Presented by Genentech Expanding Possibilities in the Treatment of Spinal Muscular Atrophy: Introducing Evrysdi™ (risdiplam) Perry Shieh, MD, PhD |
September 29 | 2:00 PM | Virtual Industry Forum: Presented by AveXis Gene therapy in the Clinic: Evolution and Clinical Considerations Diana Bharucha-Goebel Arthur Burghes Petra Kaufmann |
Once your registration is completed, a link will be provided to access our Summer Seminar Series agenda and RSVP information, Virtual Poster Library and on-demand presentations. If you have already registered for the 2020 MDA Clinical & Scientific Conference, please use this link to access these offerings and archived content. Your RSVP is required to gain access to our upcoming programs.
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